国产精品99一区二区三_免费中文日韩_国产在线精品一区二区_日本成人手机在线

Aussie researchers roll out major gene therapy program to help kids with liver disease

Source: Xinhua| 2018-11-16 09:27:02|Editor: Shi Yinglun
Video PlayerClose

SYDNEY, Nov. 16 (Xinhua) -- Australian researchers on Friday rolled out a major gene therapy treatment program aimed at saving children suffering from life-threatening genetic liver disease.

The program involves the development of new viral vectors, which transport a healthy copy of a gene into a patient's cells to either replace or edit faulty ones, the Children's Medical Research Institute said in a statement.

"We're trying to get to a point where instead of a liver transplant in a very young infant, we can genetically repair the liver without major surgery." said program leader Professor Ian Alexander.

"This technology could translate into saving the lives of infants with life-threatening conditions. It's about getting cures into the clinic as soon as we can."

The program is in line with a broad-ranging New South Wales state health and medical initiative to develop gene transfer vectors, according to the institute.

"At the moment, we can routinely produce vectors in the lab, but to move to much larger clinical scales it is very costly and involves long, overseas waiting times for clinical trials," said institute researcher Dr Leszek Lisowski.

"That means the therapies are not going to be available to most of the public any time soon. We aim to change that; to reduce costs and local waiting times for trials so these cures are more widely and more quickly available.

"While the initial focus is on liver the technology has the potential to expand to other disease targets, involving the brain, the heart, kidneys, bone marrow and pancreas, for example."

TOP STORIES
EDITOR’S CHOICE
MOST VIEWED
EXPLORE XINHUANET
010020070750000000000000011100001376108201
主站蜘蛛池模板: 蓝田县| 嵊泗县| 正蓝旗| 招远市| 抚松县| 丹江口市| 罗城| 平顶山市| 罗定市| 岳西县| 临猗县| 大关县| 娱乐| 洞头县| 广平县| 三门县| 桃源县| 临泽县| 贡山| 齐齐哈尔市| 新宾| 奎屯市| 山阴县| 玉龙| 哈巴河县| 盐池县| 略阳县| 开阳县| 新田县| 阿坝县| 大英县| 安义县| 浦城县| 特克斯县| 昭觉县| 泰顺县| 海丰县| 阜南县| 安康市| 福州市| 西充县|